Partners team up for long-awaited trial of CMT4J gene therapy
Patient advocacy organizations CureCMT4J and the CMT Research Foundation (CMTRF) are teaming up with Elpida Therapeutics for a clinical trial of ELP-02, an experimental gene therapy for CMT4J, an ultra-rare form of Charcot-Marie-Tooth disease (CMT). “Our collaboration with Elpida Therapeutics and CMTRF enables us to move…