Patient advocacy organizations CureCMT4J and the CMT Research Foundation (CMTRF) are teaming up with Elpida Therapeutics for a clinical trial of ELP-02, an experimental gene therapy for CMT4J, an ultra-rare form of Charcot-Marie-Tooth disease (CMT). “Our collaboration with Elpida Therapeutics and CMTRF enables us to move…
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September is CMT Awareness Month, and organizations are working to increase visibility of Charcot-Marie-Tooth (CMT) disease — a disease that often goes unseen. “CMT is not invisible because it is rare. It is invisible because no one talks about it,” the Charcot-Marie-Tooth Association stated on its awareness month…
Becoming educated and informed about Charcot-Marie-Tooth disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your CMT journey.
There is no cure for CMT yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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