Armatus Bio will now further develop a potential gene therapy for Charcot-Marie-Tooth disease type 1A (CMT1A), aiming to…
Articles by Patricia Inácio, PhD
A gene therapy delivering instructions to produce the neurotrophin-3 (NT-3) protein to muscle cells improved muscle function and eased defects…
A new partnership is seeking to identify people with a mutation in the sorbitol dehydrogenase (SORD) gene — the cause…
The Charcot-Marie-Tooth Association (CMTA) and Addex Therapeutics are teaming up to investigate a potential oral therapy for Charcot-Marie-Tooth disease…
The CMT Research Foundation (CMTRF) is closing out its September CMT Action Month program with a virtual convention,…
Mutations in the GARS gene — found in people with Charcot-Marie-Tooth disease type 2D (CMT2D) — halt the first…
A potential gene therapy for Charcot-Marie-Tooth disease type 1A (CMT1A) has shown promising results in a two-year study using…
Scientist Jun Li has won a $246,172 grant to develop new MRI biomarkers to assess disease progression and response to…
The CMT Research Foundation has teamed up with AcuraStem and scientist Alessandra Bolino, PhD, to test potential new…
Ahead of this year’s Rare Disease Week on Capitol Hill, held virtually July 14–22, the EveryLife Foundation will…